Duchenne Expert Testemonies at eteplirsen AdCom April 25th
May 3, 2016
On Monday, April 25th, we made Duchenne history by changing forever the way patient input is considered by the FDA and the drug development world. Rare disease patients and advocates around the nation will benefit from your groundbreaking actions.
While Duchenne patients and their families know know first hand that eteplirsen works and is safe; listen to the testemonies below from world renowned Duchenne experts.
#MakeDuchenneHistory partners CDMD at UCLA compiled a great summary of the 11 hour event. Please watch here.